#GeneTherapy’s Time Has Come; These Pioneers Are Leading the Way http://blogs.plos.org/dnascience/2017/02/23/rare-disease-day-2017-talias-story/ #SNRTG #BigData… https://twitter.com/i/web/status/834798286850650112
#RareDisease Mom Gets #OrphanDrug Status for Her #GeneTherapy | http://www.businesswire.com/news/home/20170202006067/en/Lysogene-Receives-Orphan-Drug-Designation-FDA-LYS-GM101 #SNRTG #BigData #biotech… https://twitter.com/i/web/status/828642779425304578
2016 - The Year Gene Therapy Came of Age https://www.technologyreview.com/s/603206/everything-you-need-to-know-about-gene-therapys-most-promising-year/ #SNRTG #BigData #RareDisease #GeneTherapy #science… https://twitter.com/i/web/status/814760173457829888
A Deadly Rare Disease, A Glimmer of Hope http://www.sciencealert.com/activity-of-the-huntington-s-disease-gene-has-been-halted-for-6-months-in-mice #SNRTG #BigData #RareDisease #genomics #GeneTherapy https://t.co/yqjzDTquYD
A #GeneTherapy Is Born and Toasted: @DanaFarber w/ @Rbaehner | http://vector.childrenshospital.org/2016/06/cgd-gene-therapy-trial-a-decades-long-scientific-journey/ #SNRTG #BigData #RareDisease https://t.co/3ot9vuZeUQ